Factor VIII and factor IX development plans at the Paediatric - PowerPoint PPT Presentation

Mar 30, 2023 •284 likes •341 views

Factor VIII and factor IX development plans at the Paediatric Committee Overview Presented by: Thorsten Olski MD MSc PhD Scientific Officer, Paediatrics An agency of the European Union Progress development in children Factor VIII

Factor VIII and factor IX development plans at the Paediatric Committee Overview Presented by: Thorsten Olski MD MSc PhD Scientific Officer, Paediatrics An agency of the European Union
Progress – development in children • Factor VIII • Feb 2013, 86 PTP , > 12yrs; Jan 2013 50 PTP < 12yrs; Feb 2018, 25 PUP • Mar 2013, 10 PTP , > 12yrs; Sep 2015 50 PTP < 12yrs; Sep 2019, 100 PUP • June 2014, 10 PTP , > 12yrs; Mar 2016 50 PTP < 12yrs; Dec 2020, 50 PUP • Jan 2015, 8 PTP , > 12yrs; Jun 2015 50 PTP < 12yrs; May 2018, 50 PUP • Oct 2010, 50 PTP , > 12yrs; Jul 2014, 20 PUP • Sep 2011, 17 PTP , > 12yrs; Jan 2012 50 PTP < 12yrs; Feb 2016, 50 PUP • Sep 2012, 18 PTP , > 12yrs; Nov 2012 50 PTP < 12yrs; Dec 2018, 50 PUP • Dec 2016 50 PTP < 12yrs; June 2021, 100 PUP • Dec 2014 15 PTP > 12yrs; Aug 2015 50 PTP < 12yrs; Dec 2022, 50 PUP • Factor IX • July 2012, 20 PTP , > 12yrs; June 2015 20 PTP < 12yrs; 2019, 40 PUP • July 2011, 24 PTP , > 12yrs; June 2012, 12 PTP , > 12yrs; Oct 2014, 50 PTP , > 12yrs; Sep 2014 20 PTP < 12yrs; June 2017, 20 PUP • June 2013, 15 PTP , > 12yrs; Aug 2014, 20 PTP , < 12yrs; Oct 2020, 20 PUP • Jan 2011, 50 PTP , > 12yrs; Jul 2015, 20 PTP , < 12yrs; Nov 2019, 40 PUP
‘standard’ Paediatric Investigation Plan FVIII 2
Proposed ‘standard’ PIP FIX 3

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